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Let's advance gene therapy together
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Interested in collaborating on AAV gene therapy for rare diseases? We'd love to hear from you.
Partnership Opportunities
What We Bring
- Computational target validation
- AAV vector design expertise
- Deep SGCE biology knowledge
- Published research track record
What We're Looking For
- AAV vector engineering labs
- Preclinical model development
- Regulatory strategy guidance
- Patient advocacy partnerships